Cell and gene therapy for blood disorders. Modeling of novel treatment strategies for Gaucher type 1 disease and Diamond-Blackfan anemia in mice.
Författare
Summary, in English
In summary, this thesis focuses on translational and basic research evaluating novel cell and gene therapeutic strategies for GD type 1 and DBA.
Avdelning/ar
Publiceringsår
2015
Språk
Engelska
Publikation/Tidskrift/Serie
Lund University Faculty of Medicine Doctoral Dissertation Series
Volym
2015:92
Dokumenttyp
Doktorsavhandling
Förlag
Division of Molecular Medicine and Gene Therapy
Ämne
- Cell and Molecular Biology
Nyckelord
- Gaucher disease
- lentiviral vectors
- gene therapy
- Diamond-Blackfan anemia
- hematopoietic stem cells
- bone marrow transplant
- Schlafen-2
Status
Published
Handledare
- Stefan Karlsson
- Ulrika Blank Savukinas
- Göran Karlsson
ISBN/ISSN/Övrigt
- ISSN: 1652-8220
- ISBN: 978-91-7619-171-2
Försvarsdatum
23 oktober 2015
Försvarstid
13:00
Försvarsplats
Segerfalk lecture hall, BMC A10, Sölvegatan 17, Lund
Opponent
- Juan Bueren (Professor)